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Feb. 13, 2022

Compound 1: a CD33 Pre-mRNA Splicing Modulator That Increases CD33 Exon 2 Skipping in Cells

compound 1

CD33 splicing modulator preclinical (neurodegeneration) from 3.1M cmpd phenotypic CD33 splicing screen ACS Med. Chem. Lett. Pfizer Inc.

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