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Jan. 17, 2022
HTT-D3: a CNS-Penetrant Molecule with HTT Lowering Activity
HTT-D3
HTT splicing modulator PD in Huntington’s disease model from HTS and optimization Nature Communications PTC Therapeutics, So. Plainfield, NJ
HTT splicing modulator PD in Huntington’s disease model from HTS and optimization Nature Communications PTC Therapeutics, So. Plainfield, NJ